Tag Archives: fails

First US attempt to cure a rare disease with genome editing fails miserably 

First US attempt to cure a rare disease with genome editing fails miserably Scientists at Sangamo attempted the first human trial of a gene-editing method to cure rare, debilitating enzyme deficiency diseases  After showing early promise, the DNA replacement failed to reduce levels of harmful unprocessed sugars  The gene replacement itself worked, but after nearly… Read More »

Alkermes' depression treatment fails to get FDA panel backing

(Reuters) – An advisory panel to the U.S. Food and Drug Administration on Thursday voted against approving Alkermes Plc’s treatment for depression in patients with an inadequate response to standard antidepressant therapies. The decision comes two days after FDA staff reviewers bit.ly/2QegxPF flagged abuse potential for the opioid-based depression treatment and raised questions on its… Read More »